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Rare Disease and Orphan Drugs Journal

           C O NT E NT S







           Topic: Advances in Neurofibromatosis - The Future is Bright



           Review

           1        The clinical landscape of cutaneous neurofibromas in neurofibromatosis type 1
                     Rebecca M. Brown

           2        Neurofibromatosis type 2-related schwannomatosis: an update
                     Donita Lightner


           Perspective


           3        From hype to hope: foundational requirements for NF1 gene therapy success
                     Elwy Okaz, Poornima Venkat, Efrén Muñoz, Ivan Baines, Kalyan Vinnakota

           4        Plexiform neurofibromas in neurofibromatosis type 1: current and emergent therapeutic strategies
                     Hannah Kim, Julia Polen, Gurcharanjeet Kaur


           Commentary

           5        Concerns for inclusive comprehensive neurofibromatosis care - looking at the LGBTQ+ community
                     Stephen W. Gilheeney

































                      Rare Disease and Orphan Drugs Journal                                               III
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