Page 17 - Read Online
P. 17
Schiffmann. Rare Dis Orphan Drugs J 2024;3:4 https://dx.doi.org/10.20517/rdodj.2023.50 Page 11 of 11
78. Khan A, Barber DL, Huang J, et al. Lentivirus-mediated gene therapy for fabry disease. Nat Commun 2021;12:1178. DOI PubMed
PMC
79. Mechtler TP, Stary S, Metz TF, et al. Neonatal screening for lysosomal storage disorders: feasibility and incidence from a nationwide
study in Austria. Lancet 2012;379:335-41. DOI
